A high-dose regimen of SMA treatment Spinraza benefits for previously treated and untreated SMA patients of all ages, per ...

Sensing her need to connect with others in the disability community, columnist Jasmine Ramos created The Friendship Circle.

Apitegromab met the main goal of boosting motor function over a year of treatment in young people with SMA type 2 or 3 in the ...

Treatment for 10 months with Spinraza (nusinersen) normalized the activity of 38 genes in adults with spinal muscular atrophy (SMA), a genetic study showed. Among the normalized genes were those ...